NTSAD Virtual Family Conference | 2021 Late Onset GM2 Research Breakout

Steve Walkley, PhD, Albert Einstein College of Medicine
LOTS Think Tank


Heather Gray-Edwards, PhD, UMass Medical School
Gene therapy studies in sheep


Camilo Toro, MD, NIH
Medications Do’s and Don’ts


Heather Lau, MD
Questions to ask your doctor about Clinical Trials


Taylor Fields, Senior VP
IntraBio clinical trial


Isabela A Batsu, MD, Global Project Head, Rare Disease and Rare Blood Disorder Development
Sanofi Genzyme: Late Onset GM2 Patient Journey poster