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Tay-Sachs, Canavan, GM1 and Sandhoff diseases

NTSAD Virtual Family Conference Research | GM1 Gangliosidosis

NTSAD Virtual Family Conference Research | GM1 Gangliosidosis Breakout

Jill MacDougall, MPH
Canavan Research Update
Gene Therapy Center, UPenn
GM1 Natural History Study

Gary Romano, MD, PhD
Passage Bio
Passage Bio Gene Therapy Program

Samantha Parker
Head of Patient and Policy Affairs
Lysogene Gene Therapy Program

Cynthia Tifft, MD, PhD
National Human Genome Research Institute (NHGRI)
NIH Gene Therapy Program

The video recording containing Dr. Tifft's slides cannot be publicly shared at this time. Listen to audio recording of her presentation here.