NTSAD Virtual Family Conference Research | GM1 Gangliosidosis Breakout
Jill MacDougall, MPH
Canavan Research Update
Gene Therapy Center, UPenn
GM1 Natural History Study
Gary Romano, MD, PhD
Passage Bio
Passage Bio Gene Therapy Program
Samantha Parker
Head of Patient and Policy Affairs
Lysogene
Lysogene Gene Therapy Program
Cynthia Tifft, MD, PhD
National Human Genome Research Institute (NHGRI)
NIH Gene Therapy Program
The video recording containing Dr. Tifft's slides cannot be publicly shared at this time. Listen to audio recording of her presentation here.