Leading the worldwide fight to treat and cure
Tay-Sachs, Canavan, GM1 and Sandhoff diseases

NTSAD Virtual Family Conference Research | GM2 Gangliosidosis (Infantile & Juvenile)

NTSAD Virtual Family Conference Research | GM2 Gangliosidosis Breakout

Jagdeep Walia, PhD, FRPPC
Queen's University
Gene Therapy Research Program

The video recording containing Dr. Walia's slides cannot be publicly shared at this time. Listen to audio recording of his presentation here

RA Session, CEO and Founder
Taysha Gene Therapies
Introduction to Taysha Gene Therapy Program

Terence R Flotte, MD
Dean of UMass Medical School of Medicine
UMass Medical School Expanded Access

Parag Meswani, PharmD
Senior VP, Commercial Strategy and Operations
Axovant Gene Therapies

Gavin Corcoran, MD
Chief R&D Officer
Axovant Gene Therapies

Axovant Gene Therapies Program

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