Are we close to a cure?
NTSAD is dedicated to finding a cure for Tay-Sachs, Sandhoff, Canavan, GM1 and all the related diseases. Founded over 63 years ago, NTSAD has been at the forefront of advancing and supporting breakthrough research through the NTSAD Research Initiative and collaborative programs.
This is an exciting and pivotal time for the NTSAD community. There are three clinical trials in process for GM1 and Late Onset Tay-Sachs and Sandhoff, with other programs in development for Canavan, GM1 and Tay-Sachs and Sandhoff diseases. Follow NTSAD on Facebook and sign up for email updates to get the latest news.
Tay-Sachs Gene Therapy Consortium
Lysosomal Storage Disease Research Consortium