Leading the worldwide fight to treat and cure
Tay-Sachs, Canavan, GM1 and Sandhoff diseases

For Researchers

Welcome to the Scientific Community

Our families' daily struggles drive us to extend our leadership in and financial support of the research that will ultimately lead to a cure. Now more than ever, the potential exists to advance science toward effective treatments.

NTSAD solicits proposals for innovative research projects that involve basic research, translational studies or clinical studies that may lead to treatments for lysosomal storage diseases or leukodystrophies impacting the central nervous system (CNS). NTSAD's Annual Request for Proposals, 2022 Pre-application will be due in February 18, 2022. Learn more: Request for Proposals (RFP) 2022

NTSAD Research Strategy

The Research Strategy was developed by our Scientific Advisory Committee, together with other experts, to achieve that goal as quickly as possible. Learn more: NTSAD Research Strategy

Scientific Meetings hosted by NTSAD

NTSAD has hosted six scientific meetings since NTSAD's Research Initiative was launched in 2002.  They have been held in conjunction with our Annual Family Conference. Learn more: Scientific Meetings hosted by NTSAD

Scientific Advisory Committee

The Scientific Advisory Committee (SAC) is comprised of world-leading experts in lysosomal and leukodystrophy disease research and clinical care.  Their fields of expertise include neurology, genetics, biomedical research, laboratory medicine and genetic counseling. Learn more: Scientific Advisory Committee

Corporate Advisory Council

The Council advises NTSAD about its efforts to direct, fund and promote the development of treatments and cures for the NTSAD family of diseases. It will counsel NTSAD in expanding its evolving partnership model, recommend research strategies and assist NTSAD in leveraging its full range of capabilities. Learn more: Corporate Advisory Council

Past Grants

NTSAD's grants are sometimes made in collaboration with partners such as the NIH and other patient advocacy groups for the allied diseases.

These grants went on to receive over $10 million in funding through NIH!  Learn more about the broad array of research grants NTSAD has funded:

2016 Research Initiative Grants

2015 Research Initiative Grants

2014 Research Initiative Grant

2012-2013 Research Initiative Grants

2011 Research Initiative Grants

2010 Research Initiative Grants

2009-2002 Grants

Funding Innovative Research

NTSAD Research Initiative
Tay-Sachs Gene Therapy Consortium
Lysosomal Storage Disease Research Consortium