Welcome to the Scientific Community
Our families' daily struggles drive us to extend our leadership in and financial support of the research that will ultimately lead to a cure. Now more than ever, the potential exists to advance science toward effective treatments.
NTSAD Research Strategy
The Research Strategy was developed by our Scientific Advisory Committee, together with other experts, to achieve that goal as quickly as possible. Learn more: NTSAD Research Strategy
Scientific Meetings hosted by NTSAD
NTSAD has hosted six scientific meetings since NTSAD's Research Initiative was launched in 2002. They have been held in conjunction with our Annual Family Conference. Learn more: Scientific Meetings hosted by NTSAD
Scientific Advisory Committee
The Scientific Advisory Committee (SAC) is comprised of world-leading experts in lysosomal and leukodystrophy disease research and clinical care. Their fields of expertise include neurology, genetics, biomedical research, laboratory medicine and genetic counseling. Learn more: Scientific Advisory Committee
Corporate Advisory Council
The Council advises NTSAD about its efforts to direct, fund and promote the development of treatments and cures for the NTSAD family of diseases. It will counsel NTSAD in expanding its evolving partnership model, recommend research strategies and assist NTSAD in leveraging its full range of capabilities. Learn more: Corporate Advisory Council
NTSAD's grants are sometimes made in collaboration with partners such as the NIH and other patient advocacy groups for the allied diseases.
- 53 grants were awarded from 2002-2016 (view .pdf Funded Research Projects 2002-2016)
- 13 of the grants were LSDRC funded projects, funded through the Lysosomal Storage Disease Research Consortium.
These grants went on to receive over $10 million in funding through NIH! Learn more about the broad array of research grants NTSAD has funded:
2016 Research Initiative Grants
2015 Research Initiative Grants
2014 Research Initiative Grant
2012-2013 Research Initiative Grants
2011 Research Initiative Grants
2010 Research Initiative Grants
Funding Innovative Research
NTSAD Research Initiative
Tay-Sachs Gene Therapy Consortium
Lysosomal Storage Disease Research Consortium