Leading the worldwide fight to treat and cure
Tay-Sachs, Canavan, GM1 and Sandhoff diseases

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    Donate Today

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    Newly Diagnosed?

    Support and mentorship is here as you cope with a diagnosis of Canavan, GM1, Sandhoff or Tay-Sachs.

  • Clinical Trials

    Clinical Trials

    Learn more about the clinical trials in development that we hope lead to effective therapies.

  • NTSAD's New Website

    NTSAD's New Website

    Check out a sneak peek into NTSAD's new website.

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    Annual Family Conference 2023

    Join the NTSAD Community from June 1-4, 2023 in Reston, Virginia.
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    We Care for Rare

    Meet Rare Families. Read More
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Latest News

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These genetics diseases are disorders caused by an abnormality in DNA. There are many types of genetic diseases. NTSAD focuses on inherited genetic diseases that fall into two groups - lysosomal storage diseases and leukodystrophies.

Family support for Tay-Sachs, Sandhoff, GM-1 and Canavan is provided by NTSAD and we work closely with patient advocacy groups dedicated to various allied diseases.

Research efforts related to all lysosomal and link to glossary leukodystrophy allied diseases are supported by NTSAD. The gained scientific knowledge is meaningful to all allied diseases because they share many biochemical traits.

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