Leading the worldwide fight to treat and cure
Tay-Sachs, Canavan, GM1 and Sandhoff diseases

Folder Tay-Sachs Gene Therapy

Semi-annual progress reports published by TSGC on gene therapy research.

Documents

pdf TSGT Progress Report Milestone I Popular

4389 downloads

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TSGT Progress Report 2014 Milestone I.pdf

document TSGT TSD sheep YR2 Lay Summary Popular

4336 downloads

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TSGT-TSD-sheep-YR2-Lay-Summary.doc

SUMMARY OF TAY-SACHS SHEEP PROJECT FOR GENERAL DISTRIBUTION (March 2013)

pdf TSGT Research Publications Popular

3129 downloads

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TSGT-Research-Publications.pdf

A list of Tay-Sachs Gene Therapy Consortium Publications

pdf TSGT TSD sheep YR1 Lay Summary Popular

3647 downloads

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TSGT-TSD-sheep-YR1-Lay-Summary.pdf

SHEEP AS A MODEL OF TAY-SACHS DISEASE LAY SUMMARY (January 2012)

pdf TSGT Progress Update January 2010 Popular

3603 downloads

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TSGT-Progress-Update_January_2010.pdf

A Progress Report (January 11, 2010) Tay-Sachs Gene Therapy Consortium

pdf TSGT Progress Update July 2010 Popular

3764 downloads

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TSGT-Progress-Update_July-2010.pdf

A Tay-Sachs Gene Therapy Consortium Progress Update (July 2010)

pdf TSGT Progress Update 7 2012 FINAL Popular

2808 downloads

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TSGT-Progress-Update_7-2012-FINAL.pdf

A Tay-Sachs Gene Therapy Consortium Progress Update (July 2012)

pdf TSGT Progress Update 12 2010 Popular

3476 downloads

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TSGT-Progress-Update_12-2010.pdf

A Tay-Sachs Gene Therapy Consortium Progress Update (December 2010)

pdf TSGT Progress Report 2 2012 FINAL Popular

4468 downloads

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TSGT-Progress-Report_2-2012-FINAL.pdf

A Tay-Sachs Gene Therapy Consortium Progress Update (February 2012)

pdf TSGT Progress Report 9 2011v1 FINAL Popular

3579 downloads

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TSGT-Progress-Report_9-2011v1-FINAL.pdf

A Tay-Sachs Gene Therapy Consortium Progress Update (September 2011)

pdf TSGT Abstract AAV Feline Model 5 2011 Popular

3676 downloads

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TSGT-Abstract-AAV-Feline-Model_5-2011.pdf

An abstract on the Dramatic Phenotypic Improvement after Adeno-Associated Virus Gene Therapy in a Feline Model of Sandhoff Disease

pdf TSGT Abstract Intracranial AAV 5 2011 Popular

3578 downloads

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TSGT-Abstract-Intracranial-AAV_5-2011.pdf

An abstract on the Long-Term Phenotypic Correction of Feline Lysosomal Storage Disease by Intracranial AAV Gene
Therapy

pdf TSGT Progress Update 3 2010 Popular

3401 downloads

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TSGT_Progress-Update_3-2010.pdf

A Tay-Sachs Gene Therapy Consortium Progress Update (March 2010)

pdf 12 month Progress Report Eichler 2 2012 Popular

2628 downloads

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12-month-Progress-Report_Eichler_2-2012.pdf

A Progress Report on the “Clinical Outcome Measures for Gene Therapy Trial in Infantile and Juvenile GM2”.

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