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1653 downloads
2019 October Aspa poster Scott DW et al Canavan BBP-12 administration study.pdf
A route of administration study of BBP-812, an AAV9-based gene therapy for the treatment of Canavan disease, in juvenile cynomolgus macaques
Scott DW, Rouse JL, Romero KB, Eclov R, Lewis TEW, Kapadia M, Mansfield G, and Beard CWAspa Therapeutics, BridgeBio, Raleigh, NC , USA
1651 downloads
2019 October Aspa reports Scott DW et al Canavan BBP-12 administration study.pdf
Aspa Therapeutics is pleased to share the news that a poster was presented on October 22, 2019 at the European Society of Gene and Cell Therapy meeting, describing an important development in gene therapy for Canavan disease.
2511 downloads
Animal-model-Canavan_TRAKA.pdf
2979 downloads
Clinical-Course-Canavan_BLEY.pdf
2791 downloads
Canavan summary Bley February 2016.pdf
Modified on 11 June 2015 4593 downloads
Guangping_Gao_Intl_Innovation_177.pdf
Genetics expert and microbiologist, Dr. Guangping Gao, details the experiences that led to him to devoting his scientific career to tackling Canavan disease, and illuminates the successeshe and his collaborators have achieved in this area.
2968 downloads
Informed consent February 2015.pdf
Modified on 29 April 2015 3234 downloads
CANAVAN Questionnaire english 2015.pdf
Your participation in this study will help us better understand Canavan disease and why patients with the same disease often have a quite different course. Such knowledge is a prerequisite for evaluating new experimental therapies and assessing the effectiveness of palliative measures. Be sure to sign and send the informed consent as well which you can download here as well.
4315 downloads
Cover Letter Canavan February 2015.pdf
Modified on 09 March 2015 12361 downloads
Canavan review article - Ahmed Gao - August 2014.pdf
Seemin S. Ahmed • Guangping Gao
Canavan disease was first described in 1931, and this review traces the progress made in the past 8 decades to understand the disease by enumerating current hypotheses and ongoing palliative measures to alleviate patient symptoms in the context of the latest advances in the field.
Modified on 22 July 2014 2987 downloads
SUMMARY_Traka_Canavan-Lay-Summary.pdf
A research summary on the Canavan disease.
Modified on 22 July 2014 2791 downloads
Progress-Report_Traka-18-month-report-Canavan.pdf
A Research Project Summary (Feb 2012)
Modified on 22 July 2014 3059 downloads
Progress-Report_Namboodiri_Canavan-tremor-model.pdf
The progress report on the effectiveness of acetate supplementation on mice/rats.
Modified on 22 July 2014 3213 downloads
Progress-Report_Gao_Canavan-gene-therapy_02-2012.pdf
A progress report on the successful rescue of early fatality of Canavan mice by single IV injections of novel gene therapeutics.
Modified on 22 July 2014 3524 downloads
Progress-Report_Gao-FINAL.pdf
The final progress report, focusing on maximizing the efficiency of gene delivery to the CNS using the AAV9 capsid by two aims.
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